Global Gene Therapy for Inherited Genetic Disorders Market 2024 by Company, Regions, Type and Application, Forecast to 2030
1 Market Overview
- 1.1 Product Overview and Scope of Gene Therapy for Inherited Genetic Disorders
- 1.2 Market Estimation Caveats and Base Year
- 1.3 Classification of Gene Therapy for Inherited Genetic Disorders by Type
- 1.3.1 Overview: Global Gene Therapy for Inherited Genetic Disorders Market Size by Type: 2019 Versus 2023 Versus 2030
- 1.3.2 Global Gene Therapy for Inherited Genetic Disorders Consumption Value Market Share by Type in 2023
- 1.3.3 Eye Disorders
- 1.3.4 Hematological Disorders
- 1.3.5 Central Nervous System Disorders
- 1.3.6 Muscular Disorders
- 1.3.7 Others
- 1.4 Global Gene Therapy for Inherited Genetic Disorders Market by Application
- 1.4.1 Overview: Global Gene Therapy for Inherited Genetic Disorders Market Size by Application: 2019 Versus 2023 Versus 2030
- 1.4.2 Hospital
- 1.4.3 Clinic
- 1.4.4 Research Institute
- 1.4.5 Others
- 1.5 Global Gene Therapy for Inherited Genetic Disorders Market Size & Forecast
- 1.6 Global Gene Therapy for Inherited Genetic Disorders Market Size and Forecast by Region
- 1.6.1 Global Gene Therapy for Inherited Genetic Disorders Market Size by Region: 2019 VS 2023 VS 2030
- 1.6.2 Global Gene Therapy for Inherited Genetic Disorders Market Size by Region, (2019-2030)
- 1.6.3 North America Gene Therapy for Inherited Genetic Disorders Market Size and Prospect (2019-2030)
- 1.6.4 Europe Gene Therapy for Inherited Genetic Disorders Market Size and Prospect (2019-2030)
- 1.6.5 Asia-Pacific Gene Therapy for Inherited Genetic Disorders Market Size and Prospect (2019-2030)
- 1.6.6 South America Gene Therapy for Inherited Genetic Disorders Market Size and Prospect (2019-2030)
- 1.6.7 Middle East and Africa Gene Therapy for Inherited Genetic Disorders Market Size and Prospect (2019-2030)
2 Company Profiles
- 2.1 BioMarin Pharmaceutical Inc.
- 2.1.1 BioMarin Pharmaceutical Inc. Details
- 2.1.2 BioMarin Pharmaceutical Inc. Major Business
- 2.1.3 BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Product and Solutions
- 2.1.4 BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Revenue, Gross Margin and Market Share (2019-2024)
- 2.1.5 BioMarin Pharmaceutical Inc. Recent Developments and Future Plans
- 2.2 bluebird bio Inc.
- 2.2.1 bluebird bio Inc. Details
- 2.2.2 bluebird bio Inc. Major Business
- 2.2.3 bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Product and Solutions
- 2.2.4 bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Revenue, Gross Margin and Market Share (2019-2024)
- 2.2.5 bluebird bio Inc. Recent Developments and Future Plans
- 2.3 Novartis AG
- 2.3.1 Novartis AG Details
- 2.3.2 Novartis AG Major Business
- 2.3.3 Novartis AG Gene Therapy for Inherited Genetic Disorders Product and Solutions
- 2.3.4 Novartis AG Gene Therapy for Inherited Genetic Disorders Revenue, Gross Margin and Market Share (2019-2024)
- 2.3.5 Novartis AG Recent Developments and Future Plans
- 2.4 Orchard Therapeutics Plc
- 2.4.1 Orchard Therapeutics Plc Details
- 2.4.2 Orchard Therapeutics Plc Major Business
- 2.4.3 Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Product and Solutions
- 2.4.4 Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Revenue, Gross Margin and Market Share (2019-2024)
- 2.4.5 Orchard Therapeutics Plc Recent Developments and Future Plans
- 2.5 Spark Therapeutics Inc.
- 2.5.1 Spark Therapeutics Inc. Details
- 2.5.2 Spark Therapeutics Inc. Major Business
- 2.5.3 Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Product and Solutions
- 2.5.4 Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Revenue, Gross Margin and Market Share (2019-2024)
- 2.5.5 Spark Therapeutics Inc. Recent Developments and Future Plans
3 Market Competition, by Players
- 3.1 Global Gene Therapy for Inherited Genetic Disorders Revenue and Share by Players (2019-2024)
- 3.2 Market Share Analysis (2023)
- 3.2.1 Market Share of Gene Therapy for Inherited Genetic Disorders by Company Revenue
- 3.2.2 Top 3 Gene Therapy for Inherited Genetic Disorders Players Market Share in 2023
- 3.2.3 Top 6 Gene Therapy for Inherited Genetic Disorders Players Market Share in 2023
- 3.3 Gene Therapy for Inherited Genetic Disorders Market: Overall Company Footprint Analysis
- 3.3.1 Gene Therapy for Inherited Genetic Disorders Market: Region Footprint
- 3.3.2 Gene Therapy for Inherited Genetic Disorders Market: Company Product Type Footprint
- 3.3.3 Gene Therapy for Inherited Genetic Disorders Market: Company Product Application Footprint
- 3.4 New Market Entrants and Barriers to Market Entry
- 3.5 Mergers, Acquisition, Agreements, and Collaborations
4 Market Size Segment by Type
- 4.1 Global Gene Therapy for Inherited Genetic Disorders Consumption Value and Market Share by Type (2019-2024)
- 4.2 Global Gene Therapy for Inherited Genetic Disorders Market Forecast by Type (2025-2030)
5 Market Size Segment by Application
- 5.1 Global Gene Therapy for Inherited Genetic Disorders Consumption Value Market Share by Application (2019-2024)
- 5.2 Global Gene Therapy for Inherited Genetic Disorders Market Forecast by Application (2025-2030)
6 North America
- 6.1 North America Gene Therapy for Inherited Genetic Disorders Consumption Value by Type (2019-2030)
- 6.2 North America Gene Therapy for Inherited Genetic Disorders Consumption Value by Application (2019-2030)
- 6.3 North America Gene Therapy for Inherited Genetic Disorders Market Size by Country
- 6.3.1 North America Gene Therapy for Inherited Genetic Disorders Consumption Value by Country (2019-2030)
- 6.3.2 United States Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 6.3.3 Canada Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 6.3.4 Mexico Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
7 Europe
- 7.1 Europe Gene Therapy for Inherited Genetic Disorders Consumption Value by Type (2019-2030)
- 7.2 Europe Gene Therapy for Inherited Genetic Disorders Consumption Value by Application (2019-2030)
- 7.3 Europe Gene Therapy for Inherited Genetic Disorders Market Size by Country
- 7.3.1 Europe Gene Therapy for Inherited Genetic Disorders Consumption Value by Country (2019-2030)
- 7.3.2 Germany Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 7.3.3 France Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 7.3.4 United Kingdom Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 7.3.5 Russia Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 7.3.6 Italy Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
8 Asia-Pacific
- 8.1 Asia-Pacific Gene Therapy for Inherited Genetic Disorders Consumption Value by Type (2019-2030)
- 8.2 Asia-Pacific Gene Therapy for Inherited Genetic Disorders Consumption Value by Application (2019-2030)
- 8.3 Asia-Pacific Gene Therapy for Inherited Genetic Disorders Market Size by Region
- 8.3.1 Asia-Pacific Gene Therapy for Inherited Genetic Disorders Consumption Value by Region (2019-2030)
- 8.3.2 China Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 8.3.3 Japan Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 8.3.4 South Korea Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 8.3.5 India Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 8.3.6 Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 8.3.7 Australia Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
9 South America
- 9.1 South America Gene Therapy for Inherited Genetic Disorders Consumption Value by Type (2019-2030)
- 9.2 South America Gene Therapy for Inherited Genetic Disorders Consumption Value by Application (2019-2030)
- 9.3 South America Gene Therapy for Inherited Genetic Disorders Market Size by Country
- 9.3.1 South America Gene Therapy for Inherited Genetic Disorders Consumption Value by Country (2019-2030)
- 9.3.2 Brazil Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 9.3.3 Argentina Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
10 Middle East & Africa
- 10.1 Middle East & Africa Gene Therapy for Inherited Genetic Disorders Consumption Value by Type (2019-2030)
- 10.2 Middle East & Africa Gene Therapy for Inherited Genetic Disorders Consumption Value by Application (2019-2030)
- 10.3 Middle East & Africa Gene Therapy for Inherited Genetic Disorders Market Size by Country
- 10.3.1 Middle East & Africa Gene Therapy for Inherited Genetic Disorders Consumption Value by Country (2019-2030)
- 10.3.2 Turkey Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 10.3.3 Saudi Arabia Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
- 10.3.4 UAE Gene Therapy for Inherited Genetic Disorders Market Size and Forecast (2019-2030)
11 Market Dynamics
- 11.1 Gene Therapy for Inherited Genetic Disorders Market Drivers
- 11.2 Gene Therapy for Inherited Genetic Disorders Market Restraints
- 11.3 Gene Therapy for Inherited Genetic Disorders Trends Analysis
- 11.4 Porters Five Forces Analysis
- 11.4.1 Threat of New Entrants
- 11.4.2 Bargaining Power of Suppliers
- 11.4.3 Bargaining Power of Buyers
- 11.4.4 Threat of Substitutes
- 11.4.5 Competitive Rivalry
12 Industry Chain Analysis
- 12.1 Gene Therapy for Inherited Genetic Disorders Industry Chain
- 12.2 Gene Therapy for Inherited Genetic Disorders Upstream Analysis
- 12.3 Gene Therapy for Inherited Genetic Disorders Midstream Analysis
- 12.4 Gene Therapy for Inherited Genetic Disorders Downstream Analysis
13 Research Findings and Conclusion
14 Appendix
- 14.1 Methodology
- 14.2 Research Process and Data Source
According to our (Global Info Research) latest study, the global Gene Therapy for Inherited Genetic Disorders market size was valued at USD million in 2023 and is forecast to a readjusted size of USD million by 2030 with a CAGR of % during review period.
In the medicine field gene therapy (also called human gene transfer) is the therapeutic delivery of nucleic acid into a patient's cells as a drug to treat disease.A genetic disorder is a genetic problem caused by one or more abnormalities formed in the genome.
The global pharmaceutical market is 1475 billion USD in 2022, growing at a CAGR of 5% during the next six years. The pharmaceutical market includes chemical drugs and biological drugs. For biologics is expected to 381 billion USD in 2022. In comparison, the chemical drug market is estimated to increase from 1005 billion in 2018 to 1094 billion U.S. dollars in 2022. The pharmaceutical market factors such as increasing demand for healthcare, technological advancements, and the rising prevalence of chronic diseases, increase in funding from private & government organizations for development of pharmaceutical manufacturing segments and rise in R&D activities for drugs. However, the industry also faces challenges such as stringent regulations, high costs of research and development, and patent expirations. Companies need to continuously innovate and adapt to these challenges to stay competitive in the market and ensure their products reach patients in need. Additionally, the COVID-19 pandemic has highlighted the importance of vaccine development and supply chain management, further emphasizing the need for pharmaceutical companies to be agile and responsive to emerging public health needs.
The Global Info Research report includes an overview of the development of the Gene Therapy for Inherited Genetic Disorders industry chain, the market status of Hospital (Eye Disorders, Hematological Disorders), Clinic (Eye Disorders, Hematological Disorders), and key enterprises in developed and developing market, and analysed the cutting-edge technology, patent, hot applications and market trends of Gene Therapy for Inherited Genetic Disorders.
Regionally, the report analyzes the Gene Therapy for Inherited Genetic Disorders markets in key regions. North America and Europe are experiencing steady growth, driven by government initiatives and increasing consumer awareness. Asia-Pacific, particularly China, leads the global Gene Therapy for Inherited Genetic Disorders market, with robust domestic demand, supportive policies, and a strong manufacturing base.
Key Features:
The report presents comprehensive understanding of the Gene Therapy for Inherited Genetic Disorders market. It provides a holistic view of the industry, as well as detailed insights into individual components and stakeholders. The report analysis market dynamics, trends, challenges, and opportunities within the Gene Therapy for Inherited Genetic Disorders industry.
The report involves analyzing the market at a macro level:
Market Sizing and Segmentation: Report collect data on the overall market size, including the revenue generated, and market share of different by Type (e.g., Eye Disorders, Hematological Disorders).
Industry Analysis: Report analyse the broader industry trends, such as government policies and regulations, technological advancements, consumer preferences, and market dynamics. This analysis helps in understanding the key drivers and challenges influencing the Gene Therapy for Inherited Genetic Disorders market.
Regional Analysis: The report involves examining the Gene Therapy for Inherited Genetic Disorders market at a regional or national level. Report analyses regional factors such as government incentives, infrastructure development, economic conditions, and consumer behaviour to identify variations and opportunities within different markets.
Market Projections: Report covers the gathered data and analysis to make future projections and forecasts for the Gene Therapy for Inherited Genetic Disorders market. This may include estimating market growth rates, predicting market demand, and identifying emerging trends.
The report also involves a more granular approach to Gene Therapy for Inherited Genetic Disorders:
Company Analysis: Report covers individual Gene Therapy for Inherited Genetic Disorders players, suppliers, and other relevant industry players. This analysis includes studying their financial performance, market positioning, product portfolios, partnerships, and strategies.
Consumer Analysis: Report covers data on consumer behaviour, preferences, and attitudes towards Gene Therapy for Inherited Genetic Disorders This may involve surveys, interviews, and analysis of consumer reviews and feedback from different by Application (Hospital, Clinic).
Technology Analysis: Report covers specific technologies relevant to Gene Therapy for Inherited Genetic Disorders. It assesses the current state, advancements, and potential future developments in Gene Therapy for Inherited Genetic Disorders areas.
Competitive Landscape: By analyzing individual companies, suppliers, and consumers, the report present insights into the competitive landscape of the Gene Therapy for Inherited Genetic Disorders market. This analysis helps understand market share, competitive advantages, and potential areas for differentiation among industry players.
Market Validation: The report involves validating findings and projections through primary research, such as surveys, interviews, and focus groups.
Market Segmentation
Gene Therapy for Inherited Genetic Disorders market is split by Type and by Application. For the period 2019-2030, the growth among segments provides accurate calculations and forecasts for consumption value by Type, and by Application in terms of value.
Market segment by Type
Eye Disorders
Hematological Disorders
Central Nervous System Disorders
Muscular Disorders
Others
Market segment by Application
Hospital
Clinic
Research Institute
Others
Market segment by players, this report covers
BioMarin Pharmaceutical Inc.
bluebird bio Inc.
Novartis AG
Orchard Therapeutics Plc
Spark Therapeutics Inc.
Market segment by regions, regional analysis covers
North America (United States, Canada, and Mexico)
Europe (Germany, France, UK, Russia, Italy, and Rest of Europe)
Asia-Pacific (China, Japan, South Korea, India, Southeast Asia, Australia and Rest of Asia-Pacific)
South America (Brazil, Argentina and Rest of South America)
Middle East & Africa (Turkey, Saudi Arabia, UAE, Rest of Middle East & Africa)
The content of the study subjects, includes a total of 13 chapters:
Chapter 1, to describe Gene Therapy for Inherited Genetic Disorders product scope, market overview, market estimation caveats and base year.
Chapter 2, to profile the top players of Gene Therapy for Inherited Genetic Disorders, with revenue, gross margin and global market share of Gene Therapy for Inherited Genetic Disorders from 2019 to 2024.
Chapter 3, the Gene Therapy for Inherited Genetic Disorders competitive situation, revenue and global market share of top players are analyzed emphatically by landscape contrast.
Chapter 4 and 5, to segment the market size by Type and application, with consumption value and growth rate by Type, application, from 2019 to 2030.
Chapter 6, 7, 8, 9, and 10, to break the market size data at the country level, with revenue and market share for key countries in the world, from 2019 to 2024.and Gene Therapy for Inherited Genetic Disorders market forecast, by regions, type and application, with consumption value, from 2025 to 2030.
Chapter 11, market dynamics, drivers, restraints, trends and Porters Five Forces analysis.
Chapter 12, the key raw materials and key suppliers, and industry chain of Gene Therapy for Inherited Genetic Disorders.
Chapter 13, to describe Gene Therapy for Inherited Genetic Disorders research findings and conclusion.